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Drug

Evolocumab

Approved · FDA / EMA
ClassSubtilisin/kexin type 9 inhibitorEmerging researchLate-stage developmentCooling momentum

Also known as Repatha.

6
Research papers
6
Active clinical trials
PCSK9
Primary target
22
Regulatory events
Latest activity
beta

Recent clinical, regulatory, research and industry developments relating to this drug.

Evolocumab in Acute Coronary Syndrome: A Double-Blind Randomized Placebo Controlled Study

Clinical trial2026-05-01Results posted · ClinicalTrials.gov

Evidence confidence

1 claim

How strongly the incorporated evidence supports specific clinical claims about this treatment. A confidence figure is a current summary of evidence strength, not a permanent verdict.

Lowers LDL cholesterol in hyperlipidaemia
59%Moderate confidence
Uncertainty ±12%Evidence coverage: HighUpdated 15 July 2026

Evidence is mixed30 supporting evidence families · 1 well-powered no-effect result

Confidence is moderated by well-powered no-effect evidence, despite broad trial support.

Profile

Identifiers & mechanism

Canonical identifiers, marketed brand names and mechanism, resolved across RxNorm, ChEMBL and ATC.

Canonical name
Evolocumab
Aliases & brands
Repatha
RxNorm CUI
1665684
ChEMBL ID
CHEMBL2364655
ATC codes
C10AX13
UNII
LKC0U3A8NJ
Primary mechanism
Subtilisin/kexin type 9 inhibitor
Regulatory jurisdictions
emafda

Pharmacology & targets

1 target

Known molecular targets and mechanisms supported by curated pharmacology databases.

INHIBITORSubtilisin/kexin type 9 inhibitor

Regulatory timeline

22 events

The complete regulatory record, grouped by authority — approvals, safety advisories and label changes. Each authority shows its most recent events; expand one to read its full history.

Approval / market entry confirmed across FDA and EMA (2015-07-172016-07-08)
Earliest approval
2015-07-17
Latest approval
2021-09-24
Authorities
FDA · EMA
Total events
22
fdaU.S. Food and Drug Administration· 21 events
2026-07-15Label change
Label change: EVOLOCUMAB (BLA125522)
Evidence ↗
2025-08-21Label change
Label change: EVOLOCUMAB (BLA125522)
Evidence ↗
2024-11-20Label change
Label change: EVOLOCUMAB (BLA125522)
Evidence ↗
emaEuropean Medicines Agency· 1 event
2015-07-17ApprovalMulti-authority
Approval: Repatha (EMA)
Indication: Hypercholesterolaemia and mixed dyslipidaemia Repatha is indicated in adults with primary hypercholesterolaemia (heterozygous familial and non-familial) or mixed dyslipidaemia, asShow full indication

Hypercholesterolaemia and mixed dyslipidaemia Repatha is indicated in adults with primary hypercholesterolaemia (heterozygous familial and non-familial) or mixed dyslipidaemia, as an adjunct to diet: in combination with a statin or statin with other lipid lowering therapies in patients unable to reach LDL-C goals with the maximum tolerated dose of a statin or, alone or in combination with other lipid-lowering therapies in patients who are statin-intolerant, or for whom a statin is contraindicated. Homozygous familial hypercholesterolaemia Repatha is indicated in adults and adolescents aged 12 years and over with homozygous familial hypercholesterolaemia in combination with other lipid-lowering therapies. Established atherosclerotic cardiovascular disease Repatha is indicated in adults with established atherosclerotic cardiovascular disease (myocardial infarction, stroke or peripheral arterial disease) to reduce cardiovascular risk by lowering LDL-C levels, as an adjunct to correction of other risk factors: in combination with the maximum tolerated dose of a statin with or without other lipid-lowering therapies or, alone or in combination with other lipid-lowering therapies in patients who are statin-intolerant, or for whom a statin is contraindicated. For study results with respect to effects on LDL-C, cardiovascular events and populations studied see section 5.1.

Evidence ↗

Data from the U.S. Food and Drug Administration (U.S. Food and Drug Administration), public domain (CC0).

Contains information from the European Medicines Agency (European Medicines Agency), © EMA, reused under CC BY 4.0.

Clinical trials

89 trials

The current development programme across all trial phases — status mix, phase distribution and the late-stage studies shaping the evidence base.

Development programme
CLINICALTRIALS.GOV · LIVE REGISTRY
89
registered trials across all phases
LATEST COMPLETION 2025
6
Active studies
4
Recruiting
63
Late-stage (III+)
57
Completed
26
Discontinued
PHASE DISTRIBUTIONn = 89
Early Phase 13Phase 13Phase 1 / 22Phase 218Phase 2 / 32Phase 334Phase 425Phase N / A2

Late-stage studies

Phase III+ trials still open or recently active — where late-stage evidence is being generated.

Recent completions

Trials that read out recently, adding to the completed evidence base.

Research activity

6 papers

Key research shaping understanding of this drug, combining the latest publications with the most influential evidence.

Publications over time
20152022
Most influential
Recent papers
Major research themes7
Anticholesteremic Agents1Atherosclerosis1Cardiovascular Diseases1Hydroxymethylglutaryl-CoA Reductase Inhibitors1Myocardial Infarction1PCSK9 Inhibitors1Stroke1
Journals, researchers & institutions
Top journals
  • Journal of clinical lipidology2
  • Arteriosclerosis, thrombosis, and vascular biology1
  • Circulation1
  • The American journal of cardiology1
  • The New England journal of medicine1
Leading researchers
  • Adiels M2
  • Andersson L2
  • Björnson E2
  • Blom DJ2
  • Borén J2
  • Giugliano RP2
  • Hakkarainen A2
  • Kahri J2
Leading institutions
free-text, unnormalised
  • HUS Medical Imaging Center2
  • Institute of Cardiovascular and Medical Sciences2
  • Aalto University School of Science1
  • Abdominal Center (S.S.1
  • Brigham and Women's Hospital1
  • Brigham and Women's Hospital and Harvard Medical School1
References & data sources
  • RxNorm (U.S. National Library of Medicine) — drug identity
  • ChEMBL (EMBL-EBI) & UniProt — pharmacology and targets
  • Europe PMC — research literature
  • ClinicalTrials.gov — clinical trials
  • Regulatory event sources are credited in the Regulatory Timeline above.