Back to discover
Drug

Venetoclax

Approved · EMA
ClassApoptosis regulator Bcl-2 inhibitorEmerging researchLate-stage development

Also known as Venclexta, 4-(4-((2-(4-chlorophenyl)-4,4-dimethylcyclohex-1-en-1-yl)methyl)piperazin-1-yl)-N-((3-nitro-4-((tetrahydro-2H-pyran-4-ylmethyl)amino)phenyl)sulfonyl)-2-(1H-pyrrolo(2,3-b)pyridin-5-yloxy)benzamide.

1
Research papers
113
Active clinical trials
Apoptosis regulator Bcl-2
Primary target
2
Regulatory events
Latest activity
beta

Recent clinical, regulatory, research and industry developments relating to this drug.

A Phase 2 Study of Venetoclax in Relapsed Classic or Variant Hairy Cell Leukemia

Clinical trial2026-07-20Results expected Q2 2027 · ClinicalTrials.gov

Phase II Study of Hyper-CVAD Plus Nelarabine in Previously Untreated T-ALL and Lymphoblastic Lymphoma

Clinical trial2026-07-15Results expected Q4 2026 · ClinicalTrials.gov

Approval: Venclyxto (EMA)

Regulatory2016-12-04EMA

Profile

Identifiers & mechanism

Canonical identifiers, marketed brand names and mechanism, resolved across RxNorm, ChEMBL and ATC.

Canonical name
Venetoclax
Aliases & brands
Venclexta4-(4-((2-(4-chlorophenyl)-4,4-dimethylcyclohex-1-en-1-yl)methyl)piperazin-1-yl)-N-((3-nitro-4-((tetrahydro-2H-pyran-4-ylmethyl)amino)phenyl)sulfonyl)-2-(1H-pyrrolo(2,3-b)pyridin-5-yloxy)benzamide
RxNorm CUI
1747556
ChEMBL ID
CHEMBL3137309
ATC codes
L01XX52
UNII
N54AIC43PW
Primary mechanism
Apoptosis regulator Bcl-2 inhibitor
Regulatory jurisdictions
emamhra

Pharmacology & targets

1 target

Known molecular targets and mechanisms supported by curated pharmacology databases.

INHIBITORApoptosis regulator Bcl-2 inhibitor

Regulatory timeline

2 events

The complete regulatory record, grouped by authority — approvals, safety advisories and label changes. Each authority shows its most recent events; expand one to read its full history.

Earliest approval
2016-12-04
Latest approval
2016-12-04
Authorities
EMA · MHRA
Total events
2
emaEuropean Medicines Agency· 1 event
2016-12-04Approval
Approval: Venclyxto (EMA)
Indication: Venclyxto in combination with obinutuzumab is indicated for the treatment of adult patients with previously untreated chronic lymphocytic leukaemia (CLL) (see section 5.1).Show full indication

Venclyxto in combination with obinutuzumab is indicated for the treatment of adult patients with previously untreated chronic lymphocytic leukaemia (CLL) (see section 5.1). Venclyxto in combination with rituximab is indicated for the treatment of adult patients with CLL who have received at least one prior therapy. Venclyxto monotherapy is indicated for the treatment of CLL: in the presence of 17p deletion or TP53 mutation in adult patients who are unsuitable for or have failed a B cell receptor pathway inhibitor, or in the absence of 17p deletion or TP53 mutation in adult patients who have failed both chemoimmunotherapy and a B-cell receptor pathway inhibitor. Venclyxto in combination with a hypomethylating agent is indicated for the treatment of adult patients with newly  diagnosed acute myeloid leukaemia (AML) who are ineligible for intensive chemotherapy.

Evidence ↗
mhraMedicines and Healthcare products Regulatory Agency· 1 event
2021-12-10Safety communicationSafety
Drug Safety Update: Venetoclax (Venclyxto▼): updated recommendations on tumour lysis syndrome (TLS)
Evidence ↗

Contains information from the European Medicines Agency (European Medicines Agency), © EMA, reused under CC BY 4.0.

Contains public sector information from the Medicines and Healthcare products Regulatory Agency (MHRA) licensed under the Open Government Licence (OGL v3).

Clinical trials

193 trials

The current development programme across all trial phases — status mix, phase distribution and the late-stage studies shaping the evidence base.

Development programme
CLINICALTRIALS.GOV · LIVE REGISTRY
193
registered trials across all phases
LATEST COMPLETION 2026
113
Active studies
76
Recruiting
29
Late-stage (III+)
37
Completed
43
Discontinued
PHASE DISTRIBUTIONn = 193
Early Phase 12Phase 141Phase 1 / 239Phase 282Phase 2 / 35Phase 320Phase 42Phase N / A2

Late-stage studies

Phase III+ trials still open or recently active — where late-stage evidence is being generated.

Recent completions

Trials that read out recently, adding to the completed evidence base.

Research activity

1 papers

Key research shaping understanding of this drug, combining the latest publications with the most influential evidence.

Major research themes2
Antineoplastic Agents1Neoplasms1
Journals, researchers & institutions
Top journals
  • Cancer discovery1
Leading researchers
  • Amon L1
  • Bigenwald C1
  • Buqué A1
  • Chen H1
  • Dudziak D1
  • Dutertre CA1
  • Galluzzi L1
  • Kepp O1
Leading institutions
free-text, unnormalised
  • Caryl and Israel Englander Institute for Precision Medicine1
  • Center of Clinical Investigations in Biotherapies of Cancer (CICBT) 14281
  • Centre de Recherche des Cordeliers1
  • Comprehensive Cancer Center Erlangen1
  • Institut du Cancer Paris CARPEM1
  • Institut Gustave Roussy1
References & data sources
  • RxNorm (U.S. National Library of Medicine) — drug identity
  • ChEMBL (EMBL-EBI) & UniProt — pharmacology and targets
  • Europe PMC — research literature
  • ClinicalTrials.gov — clinical trials
  • Regulatory event sources are credited in the Regulatory Timeline above.