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Protein / target

Coagulation factor VIII

Encoded byF8P00451Homo sapiensSwiss-Prot
Clinically validated
Therapeutic maturity
12
Approved medicines
Open Targets target-level
View by indication →
30
Clinical trials
Small-molecule tractable
Druggability
Structure with Ligand

Protein at a glance

Biological role

Oxidoreductase

Strongest disease association

Hemophilia A

Via encoding gene F8 · Genetic evidence · score 0.99

Therapeutic position

Established drug target

Antibodies

Research activity

Emerging research

2 papers · latest 2022

Derived from structured UniProt, Open Targets and literature data on this page.

Protein profile

UniProt 2026_02

Canonical identity and biological annotation from UniProt.

Function overview

Factor VIII, along with calcium and phospholipid, acts as a cofactor for F9/factor IXa when it converts F10/factor X to the activated form, factor Xa

Subcellular location

Secreted, extracellular space
Domains and Gene Ontology detail (24)

Domains & features

F5/8 type A 1Plastocyanin-like 1Plastocyanin-like 2F5/8 type A 2Plastocyanin-like 3Plastocyanin-like 4F5/8 type A 3Plastocyanin-like 5Plastocyanin-like 6F5/8 type C 1F5/8 type C 2

Gene Ontology

  • CCOPII-coated ER to Golgi transport vesicle
  • Cendoplasmic reticulum lumen
  • Cendoplasmic reticulum-Golgi intermediate compartment membrane
  • Cextracellular region
  • Cextracellular space
  • CGolgi lumen
  • Cplasma membrane
  • Cplatelet alpha granule lumen
  • Fcopper ion binding
  • Foxidoreductase activity
  • Pacute-phase response
  • Pblood coagulation

2351 aa · 267 kDa · 2 isoforms

Biological roles

What this protein does, drawn together from its UniProt function, Gene Ontology terms and Reactome pathways.

Lipid & lipoprotein metabolismUniProtHaemostasisGO
View supporting evidence

Lipid & lipoprotein metabolism

  • ·Factor VIII, along with calcium and phospholipid, acts as a cofactor for F9/factor IXa w…

Haemostasis

  • ·platelet alpha granule lumen
  • ·blood coagulation
  • ·blood coagulation, intrinsic pathway

Concepts derived from UniProt GO Reactome — each badge above shows which sources supported that role.

Approved medicines with mapped indications

5 medicines · 1 area

Approved therapies targeting this protein, grouped by what they are approved to treat — the disease-first view of the medicines below. Relationships come from the canonical approved-indication graph (ChEMBL phase-4), the same source as the drug cards.

12 medicines meet Open Targets' target-level approved-medicine definition; the 5 shown here are those on this page with a canonical approved disease indication in the graph. Approved indications from ChEMBL (phase-4), via the canonical drug→disease graph.

Drugs targeting this protein

5

How approved and investigational drugs engage this protein — mechanism and action type, direct vs complex targeting, and how broadly each acts across other targets. A drug-first view (the section above groups the approved ones disease-first); direct binders with few recorded targets are listed first.

Turoctocog alfa pegol
Narrow target profileApprovedExogenous protein

Coagulation factor VIII exogenous protein

Indicated for Hemophilia A

Direct interaction with this protein · Only this protein recorded as a target

damoctocog alfa pegol
Narrow target profileApprovedExogenous protein

Coagulation factor VIII exogenous protein

Indicated for Hemophilia A

Direct interaction with this protein · Only this protein recorded as a target

efmoroctocog alfa
Narrow target profileApprovedExogenous protein

Coagulation factor VIII exogenous protein

Indicated for Hemophilia A

Direct interaction with this protein · Only this protein recorded as a target

lonoctocog alfa
Narrow target profileApprovedExogenous protein

Coagulation factor VIII exogenous protein

Indicated for Hemophilia A

Direct interaction with this protein · Only this protein recorded as a target

turoctocog alfa
Narrow target profileApprovedExogenous protein

Coagulation factor VIII exogenous protein

Indicated for Hemophilia A

Direct interaction with this protein · Only this protein recorded as a target

ChEMBL mechanism, action type, target identity and approved indications. Open Targets clinical status.

Translational evidence

Open Targets 26

Why this target matters therapeutically, strongest evidence first. Disease associations are gene-level (via the gene that encodes this protein) and open into the full confidence synthesis; the development universe, tractability and safety annotations are target-level, from Open Targets.

Strongest disease associations · via encoding gene F8

Gene-level evidence surfaced through the gene F8that encodes this protein — not a direct protein–disease relationship. Ranked by Forefront's causal-directness weighting, so genetically- and clinically-evidenced diseases lead over ones that merely share the literature.

Hemophilia A
1.00Well supported

Genetic evidence dominant · Open Targets 0.91

Hemophilia B
0.97Well supported

Genetic evidence dominant · Open Targets 0.69

Immune System Diseases
0.94Well supported

Genetic evidence dominant · Open Targets 0.57

View evidence synthesis (3)
Hemophilia AWell supported
1.00
agreement 0.901.00
Genetic44%Clinical33%Pathway17%Literature6%Genetic literaturedup

Open Targets aggregate 0.91 · 4 independent evidence families · 1 not counted as duplicate

Hemophilia BWell supported
0.97
agreement 0.871.00
Genetic54%Clinical30%Pathway14%Literature2%

Open Targets aggregate 0.69 · 4 independent evidence families

Immune System DiseasesWell supported
0.94
agreement 0.801.00
Genetic100%Literature0%

Open Targets aggregate 0.57 · 2 independent evidence families

The evidence agreement range shows how closely the independent evidence families agree — it is not a statistical confidence interval, and nothing here is fitted to outcome data. Derived from Open Targets evidence types under Forefront weighting; the per-type scores above show the calculation.

Show all associations
Hemophilia A0.91
Hemophilia B0.69
Immune System Diseases0.57

Drug development

16 compounds recorded · 12 approved · 4 in clinical development

Open Targets' development universe — every compound recorded against the target at any stage, not all approved medicines. Distinct from the 5 drugs that target this protein in Forefront's canonical graph (5 with a mapped approved indication, shown above): these count different sets and are not a subset relation.

View all recorded compounds (10)
DAMOCTOCOG ALFA PEGOLApproval
SIMOCTOCOG ALFAApproval
EFANESOCTOCOG ALFAApproval
TUROCTOCOG ALFAApproval
SUSOCTOCOG ALFAApproval
GIROCTOCOGENE FITELPARVOVECPhase 3
OMFILOCTOCOG ALFAPhase 3
HUMAN COAGULATION FACTOR VIIIPhase 3
TUROCTOCOG ALFA PEGOLApproval
ANTIHEMOPHILIC FACTOR, PEGYLATED (MW 20000) HUMAN SEQUENCE RECOMBINANTApproval

Open Targets known-drugs universe. Drug name and highest clinical stage only — the disease relationship is NOT read from this slice (it carries trial-context noise); approved indications come from the canonical graph above.

Tractability

Small moleculesEmerging

Feasibility evidence (structure with ligand and med-quality pocket) — no clinical-stage drug of this modality recorded.

AntibodiesStrong

Advanced Clinical and GO CC high conf support this modality.

Protein degradersEmerging

Feasibility evidence (small molecule binder) — no clinical-stage drug of this modality recorded.

Other modalitiesStrong

Approved Drug support this modality.

View underlying tractability evidence (8)
SM · Structure with LigandSM · Med-Quality PocketAB · Advanced ClinicalAB · GO CC high confAB · UniProt loc med confAB · UniProt SigP or TMHMMPR · Small Molecule BinderOC · Approved Drug

Raw Open Targets tractability assessment buckets, by modality.

Clinical trials

30

Trials of drugs that target this protein — reached indirectly through those drugs, so a trial listed here studies the drug, not the protein. Ranked by active status, then clinical phase and recency, and spread across the targeting drugs.

View all trials (26)

ClinicalTrials.gov via the drug-target graph.

What's happening now

8

Recent therapeutic activity around this target — regulatory actions, clinical trials and safety signals for 5 drugs that target this protein, plus publications where such a drug is a genuine subject. Every item is reached indirectly through the drug, not the protein itself; incidental mentions (a paper that merely measures a drug) and press items are excluded.

  1. New publication2020-04-15
    Turoctocog alfa pegol provides effective management for major and minor surgical procedures in patients across all age groups with severe haemophilia A: Full data set from the pathfinder 3 and 5 phase III trials.

    Haemophilia : the official journal of the World Federation of Hemophilia · 2020 · 10 citations · Europe PMC · via Turoctocog alfa pegol

  2. Regulatory approval2019-06-20

    Approval: Esperoct (EMA)

    ema · regulatory · ema · via Turoctocog alfa pegol

  3. Regulatory approval2018-11-22

    Approval: Jivi (EMA)

    ema · regulatory · ema · via damoctocog alfa pegol

  4. Regulatory approval2017-01-04

    Approval: Afstyla (EMA)

    ema · regulatory · ema · via lonoctocog alfa

  5. Regulatory approval2015-11-18

    Approval: Elocta (EMA)

    ema · regulatory · ema · via efmoroctocog alfa

  6. New publication2015-02-12
    Impact of severe haemophilia A on patients' health status: results from the guardian(™) 1 clinical trial of turoctocog alfa (NovoEight(®) ).

    Haemophilia : the official journal of the World Federation of Hemophilia · 2015 · 7 citations · Europe PMC · via turoctocog alfa

  7. New publication2013-05-08
    Results from a large multinational clinical trial (guardian™3) using prophylactic treatment with turoctocog alfa in paediatric patients with severe haemophilia A: safety, efficacy and pharmacokinetics.

    Haemophilia : the official journal of the World Federation of Hemophilia · 2013 · 49 citations · Europe PMC · via turoctocog alfa

  8. New publication2013-05-07
    Results from a large multinational clinical trial (guardian™1) using prophylactic treatment with turoctocog alfa in adolescent and adult patients with severe haemophilia A: safety and efficacy.

    Haemophilia : the official journal of the World Federation of Hemophilia · 2013 · 69 citations · Europe PMC · via turoctocog alfa

Objective event titles are shown unmodified; the event kind and significance line are derived from structured fields. Forefront AttentionEvent stream aggregating Europe PMC Regulatory filings ClinicalTrials.gov.

Research activity

2 papers · to 2022

Papers linked directly to this protein. This is the protein's own literature — descriptor-derived papers are kept separate below.

Most cited

Rangarajan S · The New England journal of medicine · 2017

Recent

AAV5-Factor VIII Gene Transfer in Severe Hemophilia A.

Rangarajan S · The New England journal of medicine · 2017

Europe PMC papers linked directly to this protein.