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Protein / target

RAF proto-oncogene serine/threonine-protein kinase

Encoded byRAF1P04049Homo sapiensSwiss-Prot
Clinically validated
Therapeutic maturity
4
Approved medicines
Open Targets target-level
View by indication →
30
Clinical trials
Small-molecule tractable
Druggability
Approved Drug

Protein at a glance

Biological role

Protein serine/threonine kinase

Strongest disease association

RASopathy

Via encoding gene RAF1 · Genetic evidence · score 0.96

Therapeutic position

Established drug target

Small molecules

Derived from structured UniProt, Open Targets and literature data on this page.

Protein profile

UniProt 2026_02

Canonical identity and biological annotation from UniProt.

Function overview

Serine/threonine-protein kinase that acts as a regulatory link between the membrane-associated Ras GTPases and the MAPK/ERK cascade, and this critical regulatory link functions as a switch determining cell fate decisions including proliferation, differentiation, apoptosis, survival and oncogenic tra…

View complete UniProt function annotation

Serine/threonine-protein kinase that acts as a regulatory link between the membrane-associated Ras GTPases and the MAPK/ERK cascade, and this critical regulatory link functions as a switch determining cell fate decisions including proliferation, differentiation, apoptosis, survival and oncogenic transformation. RAF1 activation initiates a mitogen-activated protein kinase (MAPK) cascade that comprises a sequential phosphorylation of the dual-specific MAPK kinases (MAP2K1/MEK1 and MAP2K2/MEK2) and the extracellular signal-regulated kinases (MAPK3/ERK1 and MAPK1/ERK2). The phosphorylated form of RAF1 (on residues Ser-338 and Ser-339, by PAK1) phosphorylates BAD/Bcl2-antagonist of cell death at 'Ser-75'. Phosphorylates adenylyl cyclases: ADCY2, ADCY5 and ADCY6, resulting in their activation. Phosphorylates PPP1R12A resulting in inhibition of the phosphatase activity. Phosphorylates TNNT2/cardiac muscle troponin T. Can promote NF-kB activation and inhibit signal transducers involved in motility (ROCK2), apoptosis (MAP3K5/ASK1 and STK3/MST2), proliferation and angiogenesis (RB1). Can protect cells from apoptosis also by translocating to the mitochondria where it binds BCL2 and displaces BAD/Bcl2-antagonist of cell death. Regulates Rho signaling and migration, and is required for normal wound healing. Plays a role in the oncogenic transformation of epithelial cells via repression of the TJ protein, occludin (OCLN) by inducing the up-regulation of a transcriptional repressor SNAI2/SLUG, which induces down-regulation of OCLN. Restricts caspase activation in response to selected stimuli, notably Fas stimulation, pathogen-mediated macrophage apoptosis, and erythroid differentiation

Subcellular location

CytoplasmCell membraneMitochondrionNucleus
Domains and Gene Ontology detail (39)

Domains & features

RBDProtein kinase

Gene Ontology

  • Ccytoplasm
  • Ccytosol
  • CGolgi apparatus
  • Cmitochondrial outer membrane
  • Cmitochondrion
  • Cnucleus
  • Cplasma membrane
  • Cpseudopodium
  • Fadenylate cyclase activator activity
  • FATP binding
  • Fenzyme binding
  • Fidentical protein binding

648 aa · 73 kDa · 2 isoforms

Biological roles

Reactome v97

What this protein does, drawn together from its UniProt function, Gene Ontology terms and Reactome pathways.

Receptor tyrosine kinase signallingGOGrowth-factor signallingGOCell proliferation & survivalGOOncogenic signallingUniProtApoptosis & cell deathUniProt · GO
View supporting evidence

Receptor tyrosine kinase signalling

  • ·ERBB2-ERBB3 signaling pathway

Growth-factor signalling

  • ·insulin-like growth factor receptor signaling pathway

Cell proliferation & survival

  • ·negative regulation of cell population proliferation

Oncogenic signalling

  • ·Serine/threonine-protein kinase that acts as a regulatory link between the membrane-asso…

Apoptosis & cell death

  • ·Serine/threonine-protein kinase that acts as a regulatory link between the membrane-asso…
  • ·apoptotic process
  • ·negative regulation of apoptotic process
  • ·regulation of apoptotic process
View underlying pathways (17)

Concepts derived from UniProt GO Reactome — each badge above shows which sources supported that role.

Interaction neighbourhood

STRING v12.0

Proteins with the strongest functional or physical association. Node size and line weight reflect STRING confidence; hover or select a partner to inspect one association.

RAP1AYWHAZHRASMAP2K1BRAFKSR1NRASKRASYWHAHYWHABRAF1

10 strongest partners — larger node and heavier line mean higher confidence

Functional and physical associations from STRING v12.0. Only associations with this protein are drawn — partner-to-partner links are not part of this evidence.

Approved medicines with mapped indications

2 medicines · 3 areas

Approved therapies targeting this protein, grouped by what they are approved to treat — the disease-first view of the medicines below. Relationships come from the canonical approved-indication graph (ChEMBL phase-4), the same source as the drug cards.

Colorectal Neoplasms1 medicine
Glioma1 medicine
Broader indication categories (1)
Neoplasms1 medicine

Broad umbrella indications (e.g. “Neoplasms”). Shown here because every medicine also appears under a more specific disease above — kept for completeness, de-emphasised for clarity.

4 medicines meet Open Targets' target-level approved-medicine definition; the 2 shown here are those on this page with a canonical approved disease indication in the graph. Approved indications from ChEMBL (phase-4), via the canonical drug→disease graph.

Drugs targeting this protein

2

How approved and investigational drugs engage this protein — mechanism and action type, direct vs complex targeting, and how broadly each acts across other targets. A drug-first view (the section above groups the approved ones disease-first); direct binders with few recorded targets are listed first.

regorafenib
ApprovedInhibitor

Serine/threonine-protein kinase RAF inhibitor

Indicated for Colorectal Neoplasms, Neoplasms

Direct interaction with this protein · 1 of 18 recorded protein targets — broad pharmacology

tovorafenib
ApprovedInhibitor

RAF serine/threonine protein kinase inhibitor

Indicated for Glioma

Acts on a complex — shared with BRAF, ARAF · 1 of 3 recorded protein targets — narrow recorded profile

ChEMBL mechanism, action type, target identity and approved indications. Open Targets clinical status.

Translational evidence

Open Targets 26

Why this target matters therapeutically, strongest evidence first. Disease associations are gene-level (via the gene that encodes this protein) and open into the full confidence synthesis; the development universe, tractability and safety annotations are target-level, from Open Targets.

Strongest disease associations · via encoding gene RAF1

Gene-level evidence surfaced through the gene RAF1that encodes this protein — not a direct protein–disease relationship. Ranked by Forefront's causal-directness weighting, so genetically- and clinically-evidenced diseases lead over ones that merely share the literature.

Noonan syndrome
0.97Well supported

Genetic evidence dominant · Open Targets 0.87

RASopathy
0.96Well supported

Genetic evidence dominant · Open Targets 0.68

Noonan syndrome 5
0.94Well supported

Genetic evidence dominant · Open Targets 0.76

LEOPARD syndrome 2
0.91Well supported

Genetic evidence dominant · Open Targets 0.71

Cardiomyopathy, Dilated
0.88Well supported

Genetic evidence dominant · Open Targets 0.69

View evidence synthesis (5)
Noonan syndromeWell supported
0.97
agreement 0.861.00
Genetic59%Pathway24%Animal model13%Literature5%Genetic literaturedup

Open Targets aggregate 0.87 · 4 independent evidence families · 1 not counted as duplicate

RASopathyWell supported
0.96
agreement 0.821.00
Genetic97%Literature3%Genetic literaturedup

Open Targets aggregate 0.68 · 2 independent evidence families · 1 not counted as duplicate

Noonan syndrome 5Well supported
0.94
agreement 0.821.00
Genetic85%Animal model14%Literature1%Genetic literaturedup

Open Targets aggregate 0.76 · 3 independent evidence families · 1 not counted as duplicate

LEOPARD syndrome 2Well supported
0.91
agreement 0.791.00
Genetic87%Animal model13%Literature1%Genetic literaturedup

Open Targets aggregate 0.71 · 3 independent evidence families · 1 not counted as duplicate

Cardiomyopathy, DilatedWell supported
0.88
agreement 0.760.99
Genetic84%Animal model15%Literature1%Genetic literaturedup

Open Targets aggregate 0.69 · 3 independent evidence families · 1 not counted as duplicate

The evidence agreement range shows how closely the independent evidence families agree — it is not a statistical confidence interval, and nothing here is fitted to outcome data. Derived from Open Targets evidence types under Forefront weighting; the per-type scores above show the calculation.

Show all associations
Noonan syndrome0.87
Noonan syndrome with multiple lentigines0.78
Noonan syndrome 50.76
LEOPARD syndrome 20.71
Cardiomyopathy, Dilated0.69
RASopathy0.68
Carcinoma, Hepatocellular0.67
Neoplasms0.63
Carcinoma, Renal Cell0.58
Colorectal Neoplasms0.58

Drug development

9 compounds recorded · 4 approved · 5 in clinical development

Open Targets' development universe — every compound recorded against the target at any stage, not all approved medicines. Distinct from the 2 drugs that target this protein in Forefront's canonical graph (2 with a mapped approved indication, shown above): these count different sets and are not a subset relation.

View all recorded compounds (9)
BELVARAFENIBPhase 2
LY-3009120Phase 1
XL-281Phase 1 2
SORAFENIB TOSYLATEApproval
REGORAFENIBApproval
ARQ-736Phase 1
SORAFENIBApproval
TOVORAFENIBApproval
NAPORAFENIBPhase 3

Open Targets known-drugs universe. Drug name and highest clinical stage only — the disease relationship is NOT read from this slice (it carries trial-context noise); approved indications come from the canonical graph above.

Tractability

Small moleculesStrong

Approved Drug and Structure with Ligand support this modality.

AntibodiesEmerging

Feasibility evidence (go cc high conf and uniprot loc med conf) — no clinical-stage drug of this modality recorded.

Protein degradersEmerging

Feasibility evidence (database ubiquitination and half-life data) — no clinical-stage drug of this modality recorded.

View underlying tractability evidence (11)
SM · Approved DrugSM · Structure with LigandSM · High-Quality LigandSM · High-Quality PocketSM · Druggable FamilyAB · GO CC high confAB · UniProt loc med confAB · Human Protein Atlas locPR · Database UbiquitinationPR · Half-life DataPR · Small Molecule Binder

Raw Open Targets tractability assessment buckets, by modality.

Safety-related annotations

regulation of catalytic activityToxCastheart diseaseForce et al. (2011)

Terms indexed against this target in Open Targets' safety data, with their datasource. These are annotations, not causal claims: the direction of effect (whether activation or inhibition is implicated), species and evidence strength are not captured here, so an entry does not mean that modulating this target is known to cause that condition.

Clinical trials

30

Trials of drugs that target this protein — reached indirectly through those drugs, so a trial listed here studies the drug, not the protein. Ranked by active status, then clinical phase and recency, and spread across the targeting drugs.

View all trials (26)

ClinicalTrials.gov via the drug-target graph.

What's happening now

7

Recent therapeutic activity around this target — regulatory actions, clinical trials and safety signals for 2 drugs that target this protein, plus publications where such a drug is a genuine subject. Every item is reached indirectly through the drug, not the protein itself; incidental mentions (a paper that merely measures a drug) and press items are excluded.

  1. Regulatory approval2026-04-20

    Approval: Ojemda (EMA)

    ema · regulatory · ema · via tovorafenib

  2. New publication2024-06-04
    Lenvatinib Plus Pembrolizumab Versus Standard of Care for Previously Treated Metastatic Colorectal Cancer: Final Analysis of the Randomized, Open-Label, Phase III LEAP-017 Study.

    Journal of clinical oncology : official journal of the American Society of Clinical Oncology · 2024 · 69 citations · Europe PMC · via regorafenib

  3. New publication2020-08-11
    Targeted therapy for hepatocellular carcinoma.

    Signal transduction and targeted therapy · 2020 · 565 citations · Europe PMC · via regorafenib

  4. New publication2019-11-04
    Molecular targeted and immune checkpoint therapy for advanced hepatocellular carcinoma.

    Journal of experimental & clinical cancer research : CR · 2019 · 162 citations · Europe PMC · via regorafenib

  5. New publication2019-04-23
    Randomized Double-Blind Phase II Study of Regorafenib in Patients With Metastatic Osteosarcoma.

    Journal of clinical oncology : official journal of the American Society of Clinical Oncology · 2019 · 199 citations · Europe PMC · via regorafenib

  6. New publication2016-12-06
    Regorafenib for patients with hepatocellular carcinoma who progressed on sorafenib treatment (RESORCE): a randomised, double-blind, placebo-controlled, phase 3 trial.

    Lancet (London, England) · 2017 · 2,767 citations · Europe PMC · via regorafenib

  7. Regulatory approval2013-08-26

    Approval: Stivarga (EMA)

    ema · regulatory · ema · via regorafenib

Objective event titles are shown unmodified; the event kind and significance line are derived from structured fields. Forefront AttentionEvent stream aggregating Europe PMC Regulatory filings ClinicalTrials.gov.