Protein / target

Kinesin-1 heavy chain

KIF5BP33176Homo sapiensSwiss-Prot
Clinically validated
Therapeutic maturity
2
Approved medicines
11
Clinical trials
Small-molecule tractable
Druggability
Approved Drug

Protein at a glance

Biological role

Plus-end-directed microtubule motor activity

Primary system

Nervous system

Strongest disease association

kyphomelic dysplasia

Genetic literature evidence · score 0.79

Therapeutic maturity

Clinically validated target

2 approved medicines against this target

Druggability

Small molecule

Open Targets tractability · Approved Drug

Clinical development

2 approved

11 linked trials

Derived from structured UniProt, Open Targets and literature data on this page.

Protein profile

UniProt 2026_02

Canonical identity and biological annotation from UniProt.

Function

Microtubule-dependent motor required for normal distribution of mitochondria and lysosomes. Can induce formation of neurite-like membrane protrusions in non-neuronal cells in a ZFYVE27-dependent manner (By similarity). Regulates centrosome and nuclear positioning during mitotic entry. During the G2 phase of the cell cycle in a BICD2-dependent manner, antagonizes dynein function and drives the separation of nuclei and centrosomes (PubMed:20386726). Required for anterograde axonal transportation of MAPK8IP3/JIP3 which is essential for MAPK8IP3/JIP3 function in axon elongation (By similarity). Through binding with PLEKHM2 and ARL8B, directs lysosome movement toward microtubule plus ends (Probable). Involved in NK cell-mediated cytotoxicity. Drives the polarization of cytolytic granules and microtubule-organizing centers (MTOCs) toward the immune synapse between effector NK lymphocytes and target cells (PubMed:24088571)

Subcellular location

Cytoplasm, cytoskeletonCytolytic granule membraneLysosome membrane
Domains and Gene Ontology detail (40)

Domains & features

Kinesin motor

Gene Ontology

  • Caxon cytoplasm
  • Cciliary rootlet
  • Ccytolytic granule membrane
  • Ccytoplasm
  • Ccytosol
  • Cdendrite cytoplasm
  • Ckinesin complex
  • Cmembrane
  • Cmicrotubule
  • Cmitochondrion
  • Cperinuclear region of cytoplasm
  • Cphagocytic vesicle

963 aa · 110 kDa

Biological roles

Reactome v97

What this protein does, drawn together from its UniProt function, Gene Ontology terms and Reactome pathways.

Synaptic signallingUniProt · GOImmune signallingUniProt · ReactomeInhibitory neurotransmissionGO
View supporting evidence

Synaptic signalling

  • ·Microtubule-dependent motor required for normal distribution of mitochondria and lysosom…
  • ·postsynaptic cytosol
  • ·anterograde dendritic transport of neurotransmitter receptor complex
  • ·positive regulation of synaptic transmission, GABAergic

Immune signalling

  • ·Microtubule-dependent motor required for normal distribution of mitochondria and lysosom…
  • ·MHC class II antigen presentation
  • ·Processing of antigen in germinal center B cells

Inhibitory neurotransmission

  • ·positive regulation of synaptic transmission, GABAergic
View underlying pathways (7)

Concepts derived from UniProt GO Reactome — each badge above shows which sources supported that role.

Interaction neighbourhood

STRING v12.0

Proteins with the strongest functional or physical association. Node size and line weight reflect STRING confidence; hover or select a partner to inspect one association.

KLC3KLC2KLC1KLC4RANBP2KIF5ASYBUKIF5CTUBA1ATUBB2AKIF5B

10 strongest partners — larger node and heavier line mean higher confidence

Functional and physical associations from STRING v12.0. Only associations with this protein are drawn — partner-to-partner links are not part of this evidence.

Drugs targeting this protein

1

Whether each drug engages this protein directly or through a complex, and how many other targets are recorded for it. Direct binders with few recorded targets are listed first.

pralsetinib
Narrow target profileApprovedInhibitor

Kinesin-1 heavy chain/ Tyrosine-protein kinase receptor RET inhibitor

Appears in clinical studies involving medullary thyroid gland carcinoma, non-small cell lung carcinoma, non-small cell lung carcinoma, neoplasm

Direct interaction with this protein · 1 of 3 recorded protein targets — narrow recorded profile

ChEMBL mechanism, action type and target identity. Open Targets clinical status and indications.

Translational evidence

Open Targets 26

Why this target matters therapeutically — disease associations, drugs in development, tractability and safety, from Open Targets.

Strongest genetic associations

Human genetic evidence — the most direct causal link between this target and a disease.

kyphomelic dysplasia0.79

Genetic literature · overall 0.49

Intellectual disability0.70

Genetic · overall 0.47

Severe muscular hypotonia0.70

Genetic · overall 0.43

Global developmental delay0.67

Genetic · overall 0.41

Highest-confidence therapeutic associations

Diseases where a drug acting on this target has already reached clinical development.

non-small cell lung carcinoma0.95

Clinical · overall 0.67

medullary thyroid gland carcinoma0.88

Clinical · overall 0.54

thyroid cancer0.78

Clinical · overall 0.48

neoplasm0.77

Clinical · overall 0.50

cancer0.09

Clinical · overall 0.58

Highest overall evidence

Remaining associations by Open Targets' aggregated evidence score.

neurodegenerative disease0.41

Pathway

Show all associations
non-small cell lung carcinoma0.67
cancer0.58
medullary thyroid gland carcinoma0.54
neoplasm0.50
kyphomelic dysplasia0.49
thyroid cancer0.48
Intellectual disability0.47
Severe muscular hypotonia0.43
neurodegenerative disease0.41
Global developmental delay0.41

Open Targets ranks 321 associations for this target and we store the top 10 by aggregated score. The long tail is largely literature co-mention and RNA-expression evidence, not evidence that this target drives those diseases.

Known drugs · 2 total

PRALSETINIBApproval

medullary thyroid gland carcinoma · non-small cell lung carcinoma · non-small cell lung carcinoma

SELPERCATINIBApproval

medullary thyroid gland carcinoma · non-small cell lung carcinoma · thyroid cancer

Tractability

SM · Approved DrugSM · Structure with LigandSM · High-Quality LigandSM · Med-Quality PocketAB · UniProt loc high confPR · UniProt UbiquitinationPR · Database UbiquitinationPR · Half-life DataPR · Small Molecule Binder

Clinical trials

11

Trials of drugs that target this protein — reached indirectly through those drugs, so a trial listed here studies the drug, not the protein.

ClinicalTrials.gov via the drug-target graph.

Forefront confidence

Synthesis

Our own weighting of the evidence behind each disease association. Human genetics and clinical evidence count for most; literature co-mention counts for little, because two entities sharing an abstract is not evidence that one drives the other.

non-small cell lung carcinomaWell supported
0.83
agreement 0.710.95
Clinical61%Somatic mutation34%Literature5%

Open Targets aggregate 0.67 · 3 independent evidence families

Intellectual disabilityModerately supported
0.70
agreement 0.580.82
Genetic100%Genetic literaturedup

Open Targets aggregate 0.47 · 1 independent evidence family · 1 not counted as duplicate

Severe muscular hypotoniaModerately supported
0.70
agreement 0.580.82
Genetic100%

Open Targets aggregate 0.43 · 1 independent evidence family

Global developmental delayModerately supported
0.67
agreement 0.530.81
Genetic100%Literature1%

Open Targets aggregate 0.41 · 2 independent evidence families

medullary thyroid gland carcinomaModerately supported
0.66
agreement 0.510.82
Clinical99%Literature1%

Open Targets aggregate 0.54 · 2 independent evidence families

The evidence agreement range shows how closely the independent evidence families agree — it is not a statistical confidence interval, and nothing here is fitted to outcome data. Derived from Open Targets evidence types under Forefront weighting; the underlying per-type scores are shown above so the calculation can be checked.

What's happening now

2

Recent activity around this target, drawn from one canonical event stream. Every item is reached through a drug that targets this protein, so each event is news about that drug rather than about the protein directly.

  1. Withdrawn from market2024-10-24

    Market withdrawal: Gavreto (EMA)

    ema · market · ema · via pralsetinib

  2. New publication2024-01-01
    Pralsetinib in Patients with Advanced/Metastatic Rearranged During Transfection (RET)-Altered Thyroid Cancer: Updated Efficacy and Safety Data from the ARROW Study.

    Thyroid : official journal of the American Thyroid Association · 2024 · 40 citations · Europe PMC · via pralsetinib

Objective event titles are shown unmodified; the event kind and significance line are derived from structured fields. Forefront AttentionEvent stream aggregating Europe PMC Regulatory filings ClinicalTrials.gov.