Protein / target

Folate receptor alpha

FOLR1P15328Homo sapiensSwiss-Prot
Clinically validated
Therapeutic maturity
2
Approved medicines
20
Clinical trials
Small-molecule tractable
Druggability
Structure with Ligand

Protein at a glance

Biological role

Folic acid receptor activity

Primary system

Cardiovascular system

Strongest disease association

neurodegenerative syndrome due to cerebral folate transport deficiency

Genetic evidence · score 0.86

Therapeutic maturity

Clinically validated target

2 approved medicines against this target

Druggability

Small molecule

Open Targets tractability · Structure with Ligand

Clinical development

2 approved · 2 in clinical development

20 linked trials

Derived from structured UniProt, Open Targets and literature data on this page.

Protein profile

UniProt 2026_02

Canonical identity and biological annotation from UniProt.

Function

Binds to folate and reduced folic acid derivatives and mediates delivery of 5-methyltetrahydrofolate and folate analogs into the interior of cells (PubMed:19074442, PubMed:23851396, PubMed:23934049, PubMed:2527252, PubMed:8033114, PubMed:8567728). Has high affinity for folate and folic acid analogs at neutral pH (PubMed:23851396, PubMed:23934049, PubMed:2527252, PubMed:8033114, PubMed:8567728). Exposure to slightly acidic pH after receptor endocytosis triggers a conformation change that strongly reduces its affinity for folates and mediates their release (PubMed:8567728). Required for normal embryonic development and normal cell proliferation (By similarity)

Subcellular location

Cell membraneApical cell membraneBasolateral cell membraneSecretedCytoplasmic vesicleCytoplasmic vesicle, clathrin-coated vesicleEndosome
Domains and Gene Ontology detail (34)

Gene Ontology

  • Capical plasma membrane
  • Cbasolateral plasma membrane
  • Cbrush border membrane
  • Ccell surface
  • Cclathrin-coated vesicle
  • Cendoplasmic reticulum membrane
  • Cendoplasmic reticulum-Golgi intermediate compartment membrane
  • Cendosome
  • CER to Golgi transport vesicle membrane
  • Cexternal side of plasma membrane
  • Cextracellular exosome
  • CGolgi membrane

257 aa · 30 kDa

Biological roles

Reactome v97

What this protein does, drawn together from its UniProt function, Gene Ontology terms and Reactome pathways.

Immune signallingGOCell adhesionGO
View supporting evidence

Immune signalling

  • ·cardiac neural crest cell migration involved in outflow tract morphogenesis
  • ·neural crest cell migration involved in heart formation

Cell adhesion

  • ·cell adhesion
View underlying pathways (3)

Concepts derived from UniProt GO Reactome — each badge above shows which sources supported that role.

Interaction neighbourhood

STRING v12.0

Proteins with the strongest functional or physical association. Node size and line weight reflect STRING confidence; hover or select a partner to inspect one association.

FOLH1SLC46A1PCBP1TYMSEGFRMSLNFGF3EPCAMSLC19A1TFRCFOLR1

10 strongest partners — larger node and heavier line mean higher confidence

Functional and physical associations from STRING v12.0. Only associations with this protein are drawn — partner-to-partner links are not part of this evidence.

Drugs targeting this protein

1

Whether each drug engages this protein directly or through a complex, and how many other targets are recorded for it. Direct binders with few recorded targets are listed first.

mirvetuximab soravtansine
ApprovedBinding agent

Folate receptor alpha binding agent

Appears in clinical studies involving ovarian cancer, ovarian neoplasm, fallopian tube neoplasm, peritoneal neoplasm

Direct interaction with this protein · 1 of 16 recorded protein targets — broad pharmacology

ChEMBL mechanism, action type and target identity. Open Targets clinical status and indications.

Translational evidence

Open Targets 26

Why this target matters therapeutically — disease associations, drugs in development, tractability and safety, from Open Targets.

Strongest genetic associations

Human genetic evidence — the most direct causal link between this target and a disease.

neurodegenerative syndrome due to cerebral folate transport deficiency0.86

Genetic · overall 0.81

Seizure0.61

Genetic literature · overall 0.41

Highest-confidence therapeutic associations

Diseases where a drug acting on this target has already reached clinical development.

ovarian cancer0.83

Clinical · overall 0.53

neoplasm0.77

Clinical · overall 0.50

peritoneal neoplasm0.76

Clinical · overall 0.46

fallopian tube neoplasm0.76

Clinical · overall 0.46

malignant epithelial tumor of ovary0.74

Clinical · overall 0.45

Highest overall evidence

Remaining associations by Open Targets' aggregated evidence score.

fallopian tube cancer0.39

Clinical

primary peritoneal carcinoma0.39

Clinical

ovarian neoplasm0.38

Clinical

Show all associations
neurodegenerative syndrome due to cerebral folate transport deficiency0.81
ovarian cancer0.53
neoplasm0.50
peritoneal neoplasm0.46
fallopian tube neoplasm0.46
malignant epithelial tumor of ovary0.45
Seizure0.41
fallopian tube cancer0.39
primary peritoneal carcinoma0.39
ovarian neoplasm0.38

Open Targets ranks 461 associations for this target and we store the top 10 by aggregated score. The long tail is largely literature co-mention and RNA-expression evidence, not evidence that this target drives those diseases.

Known drugs · 4 total

VINTAFOLIDEApproval

neoplasm · ovarian cancer · endometrial cancer

MIRVETUXIMABPhase 2

ovarian cancer

MIRVETUXIMAB SORAVTANSINEApproval

ovarian cancer · ovarian neoplasm · fallopian tube neoplasm

FARLETUZUMABPhase 3

non-small cell lung carcinoma · ovarian cancer · malignant epithelial tumor of ovary

Tractability

SM · Structure with LigandSM · High-Quality LigandAB · Advanced ClinicalAB · UniProt loc high confAB · UniProt SigP or TMHMMAB · GO CC med confPR · Small Molecule BinderOC · Approved Drug

Clinical trials

20

Trials of drugs that target this protein — reached indirectly through those drugs, so a trial listed here studies the drug, not the protein.

Show remaining trials (14)

ClinicalTrials.gov via the drug-target graph.

Related literature

4

Papers indexed under “Folate Receptor 1” — a subject heading that covers this protein without being specific to it. Shown as context; not counted as this protein's own research activity.

Mirvetuximab soravtansine-gynx: first antibody/antigen-drug conjugate (ADC) in advanced or recurrent ovarian cancer.

Bogani G · International journal of gynecological cancer : official journal of the International Gynecological Cancer Society · 2024

Folate Receptor Alpha-A Novel Approach to Cancer Therapy.

Gonzalez T · International journal of molecular sciences · 2024

Efficacy and Safety of Mirvetuximab Soravtansine in Patients With Platinum-Resistant Ovarian Cancer With High Folate Receptor Alpha Expression: Results From the SORAYA Study.

Matulonis UA · Journal of clinical oncology : official journal of the American Society of Clinical Oncology · 2023

Europe PMC literature, reached through a MeSH descriptor linked to this protein.

Forefront confidence

Synthesis

Our own weighting of the evidence behind each disease association. Human genetics and clinical evidence count for most; literature co-mention counts for little, because two entities sharing an abstract is not evidence that one drives the other.

neurodegenerative syndrome due to cerebral folate transport deficiencyWell supported
0.86
agreement 0.721.00
Genetic99%Literature2%Genetic literaturedup

Open Targets aggregate 0.81 · 2 independent evidence families · 1 not counted as duplicate

ovarian cancerModerately supported
0.68
agreement 0.520.83
Clinical82%Literature18%

Open Targets aggregate 0.53 · 2 independent evidence families

neoplasmModerately supported
0.64
agreement 0.480.79
Clinical80%Literature20%

Open Targets aggregate 0.50 · 2 independent evidence families

peritoneal neoplasmModerately supported
0.57
agreement 0.410.73
Clinical100%

Open Targets aggregate 0.46 · 1 independent evidence family

fallopian tube neoplasmModerately supported
0.57
agreement 0.410.73
Clinical100%

Open Targets aggregate 0.46 · 1 independent evidence family

The evidence agreement range shows how closely the independent evidence families agree — it is not a statistical confidence interval, and nothing here is fitted to outcome data. Derived from Open Targets evidence types under Forefront weighting; the underlying per-type scores are shown above so the calculation can be checked.

What's happening now

4

Recent activity around this target, drawn from one canonical event stream. Every item is reached through a drug that targets this protein, so each event is news about that drug rather than about the protein directly.

  1. New publication2024-12-03
    Analysis of real world FRα testing in ovarian, fallopian tube, and primary peritoneal cancers.

    Gynecologic oncology · 2025 · 10 citations · Europe PMC · via mirvetuximab soravtansine

  2. Regulatory approval2024-11-14

    Approval: Elahere (EMA)

    ema · regulatory · ema · via mirvetuximab soravtansine

  3. New publication2024-04-01
    Mirvetuximab soravtansine-gynx: first antibody/antigen-drug conjugate (ADC) in advanced or recurrent ovarian cancer.

    International journal of gynecological cancer : official journal of the International Gynecological Cancer Society · 2024 · 34 citations · Europe PMC · via mirvetuximab soravtansine

  4. New publication2023-01-30
    Efficacy and Safety of Mirvetuximab Soravtansine in Patients With Platinum-Resistant Ovarian Cancer With High Folate Receptor Alpha Expression: Results From the SORAYA Study.

    Journal of clinical oncology : official journal of the American Society of Clinical Oncology · 2023 · 261 citations · Europe PMC · via mirvetuximab soravtansine

Objective event titles are shown unmodified; the event kind and significance line are derived from structured fields. Forefront AttentionEvent stream aggregating Europe PMC Regulatory filings ClinicalTrials.gov.