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Protein / target

Myeloid cell surface antigen CD33

Encoded byCD33P20138Homo sapiensSwiss-Prot
Clinically validated
Therapeutic maturity
1
Approved medicines
Open Targets target-level
View by indication →
30
Clinical trials
Small-molecule tractable
Druggability
Structure with Ligand

Protein at a glance

Biological role

Protein tyrosine phosphatase activator

Strongest disease association

Alzheimer's Disease

Via encoding gene CD33 · Genetic evidence · score 0.72

Therapeutic position

Established drug target

Antibodies

Research activity

Emerging research

1 papers · latest 2016

Derived from structured UniProt, Open Targets and literature data on this page.

Protein profile

UniProt 2026_02

Canonical identity and biological annotation from UniProt.

Function overview

Sialic-acid-binding immunoglobulin-like lectin (Siglec) that plays a role in mediating cell-cell interactions and in maintaining immune cells in a resting state.

View complete UniProt function annotation

Sialic-acid-binding immunoglobulin-like lectin (Siglec) that plays a role in mediating cell-cell interactions and in maintaining immune cells in a resting state (PubMed:10611343, PubMed:11320212, PubMed:15597323). Preferentially recognizes and binds alpha-2,3- and more avidly alpha-2,6-linked sialic acid-bearing glycans (PubMed:7718872). Upon engagement of ligands such as C1q or syalylated glycoproteins, two immunoreceptor tyrosine-based inhibitory motifs (ITIMs) located in CD33 cytoplasmic tail are phosphorylated by Src-like kinases such as LCK (PubMed:10887109, PubMed:28325905). These phosphorylations provide docking sites for the recruitment and activation of protein-tyrosine phosphatases PTPN6/SHP-1 and PTPN11/SHP-2 (PubMed:10206955, PubMed:10556798, PubMed:10887109). In turn, these phosphatases regulate downstream pathways through dephosphorylation of signaling molecules (PubMed:10206955, PubMed:10887109). One of the repressive effect of CD33 on monocyte activation requires phosphoinositide 3-kinase/PI3K (PubMed:15597323)

Subcellular location

Cell membranePeroxisome
Domains and Gene Ontology detail (26)

Domains & features

Ig-like V-typeIg-like C2-type

Gene Ontology

  • Ccell surface
  • Cexternal side of plasma membrane
  • CGolgi apparatus
  • Cperoxisome
  • Cplasma membrane
  • Cspecific granule membrane
  • Ctertiary granule membrane
  • Fcarbohydrate binding
  • Fprotein phosphatase binding
  • Fprotein tyrosine phosphatase activator activity
  • Fsialic acid binding
  • Fsignaling receptor activity

364 aa · 40 kDa · 3 isoforms

Biological roles

What this protein does, drawn together from its UniProt function, Gene Ontology terms and Reactome pathways.

Cell proliferation & survivalGOImmune signallingGOCell adhesionGO
View supporting evidence

Cell proliferation & survival

  • ·negative regulation of cell population proliferation

Immune signalling

  • ·immune response-inhibiting signal transduction
  • ·negative regulation of interleukin-1 beta production
  • ·negative regulation of interleukin-8 production

Cell adhesion

  • ·cell adhesion
  • ·cell-cell adhesion

Concepts derived from UniProt GO Reactome — each badge above shows which sources supported that role.

Approved medicines with mapped indications

1 medicine · 3 areas

Approved therapies targeting this protein, grouped by what they are approved to treat — the disease-first view of the medicines below. Relationships come from the canonical approved-indication graph (ChEMBL phase-4), the same source as the drug cards.

Leukemia, Myeloid1 medicine
Leukemia, Myeloid, Acute1 medicine
Broader indication categories (1)
Neoplasms1 medicine

Broad umbrella indications (e.g. “Neoplasms”). Shown here because every medicine also appears under a more specific disease above — kept for completeness, de-emphasised for clarity.

Approved indications from ChEMBL (phase-4), via the canonical drug→disease graph.

Drugs targeting this protein

1

How approved and investigational drugs engage this protein — mechanism and action type, direct vs complex targeting, and how broadly each acts across other targets. A drug-first view (the section above groups the approved ones disease-first); direct binders with few recorded targets are listed first.

gemtuzumab ozogamicin
Narrow target profileApprovedBinding agent

Myeloid cell surface antigen CD33 binding agent

Indicated for Leukemia, Myeloid, Leukemia, Myeloid, Acute, Neoplasms

Direct interaction with this protein · Only this protein recorded as a target

ChEMBL mechanism, action type, target identity and approved indications. Open Targets clinical status.

Translational evidence

Open Targets 26

Why this target matters therapeutically, strongest evidence first. Disease associations are gene-level (via the gene that encodes this protein) and open into the full confidence synthesis; the development universe, tractability and safety annotations are target-level, from Open Targets.

Strongest disease associations · via encoding gene CD33

Gene-level evidence surfaced through the gene CD33that encodes this protein — not a direct protein–disease relationship. Ranked by Forefront's causal-directness weighting, so genetically- and clinically-evidenced diseases lead over ones that merely share the literature.

Alzheimer's Disease
0.82Well supported

Genetic evidence dominant · Open Targets 0.54

Leukemia, Myeloid, Acute
0.75Well supported

Clinical evidence dominant · Open Targets 0.61

Acute promyelocytic leukemia
0.59Moderately supported

Clinical evidence dominant · Open Targets 0.47

Neoplasms
0.53Moderately supported

Clinical evidence dominant · Open Targets 0.40

Leukemia, Myeloid
0.50Moderately supported

Clinical evidence dominant · Open Targets 0.40

View evidence synthesis (5)
Alzheimer's DiseaseWell supported
0.82
agreement 0.700.94
Genetic66%Pathway21%Literature13%

Open Targets aggregate 0.54 · 3 independent evidence families

Leukemia, Myeloid, AcuteWell supported
0.75
agreement 0.600.91
Clinical83%Literature17%

Open Targets aggregate 0.61 · 2 independent evidence families

Acute promyelocytic leukemiaModerately supported
0.59
agreement 0.440.75
Clinical88%Literature12%

Open Targets aggregate 0.47 · 2 independent evidence families

NeoplasmsModerately supported
0.53
agreement 0.380.69
Clinical76%Literature24%

Open Targets aggregate 0.40 · 2 independent evidence families

Leukemia, MyeloidModerately supported
0.50
agreement 0.350.66
Clinical95%Literature5%

Open Targets aggregate 0.40 · 2 independent evidence families

This ranking differs from Open Targets' own: re-weighting moves genetically-evidenced diseases above more heavily co-mentioned ones. The evidence agreement range shows how closely the independent evidence families agree — it is not a statistical confidence interval, and nothing here is fitted to outcome data. Derived from Open Targets evidence types under Forefront weighting; the per-type scores above show the calculation.

Show all associations
Leukemia, Myeloid, Acute0.61
Alzheimer's Disease0.54
Acute promyelocytic leukemia0.47
Leukemia, Myeloid0.40
Neoplasms0.40
Dengue0.37
Myelodysplastic syndrome0.37
Parkinson's Disease0.37
Neurodegenerative Diseases0.35

Drug development

5 compounds recorded · 1 approved · 4 in clinical development

Open Targets' development universe — every compound recorded against the target at any stage, not all approved medicines. Distinct from the 1 drug that targets this protein in Forefront's canonical graph (1 with a mapped approved indication, shown above): these count different sets and are not a subset relation.

View all recorded compounds (5)
LINTUZUMABPhase 3
GEMTUZUMABPhase 2
ONCOLYSIN MPhase 1
GEMTUZUMAB OZOGAMICINApproval
AVE-9633Phase 1

Open Targets known-drugs universe. Drug name and highest clinical stage only — the disease relationship is NOT read from this slice (it carries trial-context noise); approved indications come from the canonical graph above.

Tractability

Small moleculesEmerging

Feasibility evidence (structure with ligand) — no clinical-stage drug of this modality recorded.

AntibodiesStrong

Advanced Clinical and UniProt loc high conf support this modality.

Protein degradersEmerging

Feasibility evidence (database ubiquitination and half-life data) — no clinical-stage drug of this modality recorded.

Other modalitiesStrong

Approved Drug support this modality.

View underlying tractability evidence (9)
SM · Structure with LigandAB · Advanced ClinicalAB · UniProt loc high confAB · GO CC high confAB · UniProt SigP or TMHMMAB · Human Protein Atlas locPR · Database UbiquitinationPR · Half-life DataOC · Approved Drug

Raw Open Targets tractability assessment buckets, by modality.

Clinical trials

30

Trials of drugs that target this protein — reached indirectly through those drugs, so a trial listed here studies the drug, not the protein. Ranked by active status, then clinical phase and recency, and spread across the targeting drugs.

View all trials (26)

RECRUITING · via gemtuzumab ozogamicin · NCT05564390

ACTIVE_NOT_RECRUITING · via gemtuzumab ozogamicin · NCT05599360

RECRUITING · via gemtuzumab ozogamicin · NCT04793919

COMPLETED · via gemtuzumab ozogamicin · NCT00476541

ClinicalTrials.gov via the drug-target graph.

What's happening now

4

Recent therapeutic activity around this target — regulatory actions, clinical trials and safety signals for a drug that targets this protein, plus publications where such a drug is a genuine subject. Every item is reached indirectly through the drug, not the protein itself; incidental mentions (a paper that merely measures a drug) and press items are excluded.

  1. Trial status changed2026-07-24

    A Pilot Study of Liposomal Cytarabine and Daunorubicin (CPX-351) in Combination With Gemtuzumab Ozogamicin (GO) in Relapsed Refractory Patients With Acute Myeloid Leukemia (AML) and Post-Hypomethylating Agent (Post-HMA) Failure High-Risk Myelodysplastic Syndrome (HR-MDS)

    Status changed to Completed · ClinicalTrials.gov · via gemtuzumab ozogamicin

  2. Trial results posted2026-07-23

    Fractionated Gemtuzumab Ozogamicin Followed by Non-engraftment Donor Leukocyte Infusions for Relapsed/Refractory Acute Myeloid Leukemia

    Results posted · ClinicalTrials.gov · via gemtuzumab ozogamicin

  3. Trial status changed2026-07-23

    Fractionated Gemtuzumab Ozogamicin Followed by Non-engraftment Donor Leukocyte Infusions for Relapsed/Refractory Acute Myeloid Leukemia

    Status changed to Completed · ClinicalTrials.gov · via gemtuzumab ozogamicin

  4. Regulatory approval2018-04-19

    Approval: Mylotarg (EMA)

    ema · regulatory · ema · via gemtuzumab ozogamicin

Objective event titles are shown unmodified; the event kind and significance line are derived from structured fields. Forefront AttentionEvent stream aggregating Europe PMC Regulatory filings ClinicalTrials.gov.

Research activity

1 papers · to 2016

Papers linked directly to this protein. This is the protein's own literature — descriptor-derived papers are kept separate below.

Most cited

Recent

Europe PMC papers linked directly to this protein.