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Protein / target

26S proteasome complex subunit SEM1

Encoded bySEM1P60896Homo sapiensSwiss-Prot
Clinically validated
Therapeutic maturity
5
Approved medicines
Open Targets target-level
View by indication →
30
Clinical trials
Small-molecule tractable
Druggability
Approved Drug

Protein at a glance

Biological role

Ubiquitin binding

Strongest disease association

Osteoporosis

Via encoding gene SEM1 · Genetic evidence · score 0.56

Therapeutic position

Established drug target

Small molecules

Derived from structured UniProt, Open Targets and literature data on this page.

Protein profile

UniProt 2026_02

Canonical identity and biological annotation from UniProt.

Function overview

Component of the 26S proteasome, a multiprotein complex involved in the ATP-dependent degradation of ubiquitinated proteins.

View complete UniProt function annotation

Component of the 26S proteasome, a multiprotein complex involved in the ATP-dependent degradation of ubiquitinated proteins. This complex plays a key role in the maintenance of protein homeostasis by removing misfolded or damaged proteins, which could impair cellular functions, and by removing proteins whose functions are no longer required. Therefore, the proteasome participates in numerous cellular processes, including cell cycle progression, apoptosis, or DNA damage repair (PubMed:15117943). Component of the TREX-2 complex (transcription and export complex 2), composed of at least ENY2, GANP, PCID2, SEM1, and either centrin CETN2 or CETN3 (PubMed:22307388). The TREX-2 complex functions in docking export-competent ribonucleoprotein particles (mRNPs) to the nuclear entrance of the nuclear pore complex (nuclear basket). TREX-2 participates in mRNA export and accurate chromatin positioning in the nucleus by tethering genes to the nuclear periphery. Binds and stabilizes BRCA2 and is thus involved in the control of R-loop-associated DNA damage and thus transcription-associated genomic instability. R-loop accumulation increases in SEM1-depleted cells

Subcellular location

Nucleus
Domains and Gene Ontology detail (16)

Gene Ontology

  • Ccytosol
  • Cintegrator complex
  • Cnucleoplasm
  • Cproteasome complex
  • Cproteasome regulatory particle, lid subcomplex
  • Cprotein-containing complex
  • Csynaptic vesicle
  • Fubiquitin binding
  • Pcellular response to type I interferon
  • PmRNA export from nucleus
  • Ppositive regulation of transcription by RNA polymerase II
  • Pproteasomal protein catabolic process

70 aa · 8 kDa · 2 isoforms

Biological roles

What this protein does, drawn together from its UniProt function, Gene Ontology terms and Reactome pathways.

Transcriptional regulationUniProt · GO
View supporting evidence

Transcriptional regulation

  • ·Component of the 26S proteasome, a multiprotein complex involved in the ATP-dependent de…
  • ·positive regulation of transcription by RNA polymerase II

Concepts derived from UniProt GO Reactome — each badge above shows which sources supported that role.

Approved medicines with mapped indications

3 medicines · 2 areas

Approved therapies targeting this protein, grouped by what they are approved to treat — the disease-first view of the medicines below. Relationships come from the canonical approved-indication graph (ChEMBL phase-4), the same source as the drug cards.

Multiple Myeloma1 medicine
Neoplasms3 medicines

5 medicines meet Open Targets' target-level approved-medicine definition; the 3 shown here are those on this page with a canonical approved disease indication in the graph. Approved indications from ChEMBL (phase-4), via the canonical drug→disease graph.

Drugs targeting this protein

4

How approved and investigational drugs engage this protein — mechanism and action type, direct vs complex targeting, and how broadly each acts across other targets. A drug-first view (the section above groups the approved ones disease-first); direct binders with few recorded targets are listed first.

bortezomib
ApprovedInhibitor

26S proteasome inhibitor

Indicated for Neoplasms

Acts on a complex — shared with PSMD1, PSMB2, PSMB1 +34 more · 1 of 38 recorded protein targets — broad pharmacology

carfilzomib
ApprovedInhibitor

26S proteasome inhibitor

Indicated for Multiple Myeloma, Neoplasms

Acts on a complex — shared with PSMD1, PSMB2, PSMB1 +34 more · 1 of 38 recorded protein targets — broad pharmacology

ixazomib
ApprovedInhibitor

26S proteasome inhibitor

Indicated for Neoplasms

Acts on a complex — shared with PSMD1, PSMB2, PSMB1 +34 more · 1 of 38 recorded protein targets — broad pharmacology

Oprozomib
Phase 2Inhibitor

26S proteasome inhibitor

Acts on a complex — shared with PSMD1, PSMB2, PSMB1 +34 more · 1 of 38 recorded protein targets — broad pharmacology

ChEMBL mechanism, action type, target identity and approved indications. Open Targets clinical status.

Translational evidence

Open Targets 26

Why this target matters therapeutically, strongest evidence first. Disease associations are gene-level (via the gene that encodes this protein) and open into the full confidence synthesis; the development universe, tractability and safety annotations are target-level, from Open Targets.

Strongest disease associations · via encoding gene SEM1

Gene-level evidence surfaced through the gene SEM1that encodes this protein — not a direct protein–disease relationship. Ranked by Forefront's causal-directness weighting, so genetically- and clinically-evidenced diseases lead over ones that merely share the literature.

Multiple Myeloma
0.74Moderately supported

Clinical evidence dominant · Open Targets 0.60

Neoplasms
0.74Moderately supported

Clinical evidence dominant · Open Targets 0.55

Osteoporosis
0.56Moderately supported

Genetic evidence dominant · Open Targets 0.34

HIV Infections
0.32Preliminary

Pathway evidence dominant · Open Targets 0.47 · no direct causal or clinical evidence

View evidence synthesis (4)
Multiple MyelomaModerately supported
0.74
agreement 0.590.90
Clinical100%Literature0%

Open Targets aggregate 0.60 · 2 independent evidence families

NeoplasmsModerately supported
0.74
agreement 0.610.87
Clinical59%Pathway35%Literature6%

Open Targets aggregate 0.55 · 3 independent evidence families

OsteoporosisModerately supported
0.56
agreement 0.420.70
Genetic99%Literature1%

Open Targets aggregate 0.34 · 2 independent evidence families

HIV InfectionsPreliminary
0.32
agreement 0.140.50
Pathway93%Literature8%

Open Targets aggregate 0.47 · 2 independent evidence families · no direct causal or clinical evidence

The evidence agreement range shows how closely the independent evidence families agree — it is not a statistical confidence interval, and nothing here is fitted to outcome data. Derived from Open Targets evidence types under Forefront weighting; the per-type scores above show the calculation.

Show all associations
Multiple Myeloma0.60
Neoplasms0.55
HIV Infections0.47
Osteoporosis0.34

Drug development

6 compounds recorded · 5 approved · 1 in clinical development

Open Targets' development universe — every compound recorded against the target at any stage, not all approved medicines. Distinct from the 4 drugs that target this protein in Forefront's canonical graph (3 with a mapped approved indication, shown above): these count different sets and are not a subset relation.

View all recorded compounds (6)
BORTEZOMIBApproval
CARFILZOMIBApproval
IXAZOMIB CITRATEApproval
OPROZOMIBPhase 2
IXAZOMIBApproval
BORTEZOMIB D-MANNITOLApproval

Open Targets known-drugs universe. Drug name and highest clinical stage only — the disease relationship is NOT read from this slice (it carries trial-context noise); approved indications come from the canonical graph above.

Tractability

Small moleculesStrong

Approved Drug and Structure with Ligand support this modality.

Protein degradersEmerging

Feasibility evidence (database ubiquitination) — no clinical-stage drug of this modality recorded.

View underlying tractability evidence (4)
SM · Approved DrugSM · Structure with LigandSM · High-Quality LigandPR · Database Ubiquitination

Raw Open Targets tractability assessment buckets, by modality.

Clinical trials

30

Trials of drugs that target this protein — reached indirectly through those drugs, so a trial listed here studies the drug, not the protein. Ranked by active status, then clinical phase and recency, and spread across the targeting drugs.

View all trials (26)

ClinicalTrials.gov via the drug-target graph.

What's happening now

12

Recent therapeutic activity around this target — regulatory actions, clinical trials and safety signals for 2 drugs that target this protein, plus publications where such a drug is a genuine subject. Every item is reached indirectly through the drug, not the protein itself; incidental mentions (a paper that merely measures a drug) and press items are excluded.

  1. Trial status changed2026-07-31

    A Phase 3b, Multicenter, Open-label, Daratumumab Long-term Extension Study

    Status changed to Active, not recruiting · ClinicalTrials.gov · via carfilzomib

  2. Trial status changed2026-07-30

    64407564MMY3009: A Phase 3 Randomized Study Comparing Talquetamab in Combination With Pomalidomide (Tal-P), Talquetamab in Combination With Teclistamab (Tal-Tec), and Investigator's Choice of Either Elotuzumab, Pomalidomide, and Dexamethasone (EPd) or Pom

    Status changed to Active, not recruiting · ClinicalTrials.gov · via bortezomib

  3. Regulatory approval2026-07-20

    Approval: CARFILZOMIB (ANDA209526)

    fda · regulatory · fda · via carfilzomib

  4. Withdrawn from market2025-08-07

    Market withdrawal: Bortezomib Hospira (EMA)

    ema · market · ema · via bortezomib

  5. Safety communication2019-11-21

    Drug Safety Update: Carfilzomib (Kyprolis▼): risk of reactivation of hepatitis B virus

    mhra · safety · mhra · via carfilzomib

  6. Safety communication2019-08-19

    Drug Safety Update: Carfilzomib (Kyprolis▼): reminder of risk of potentially fatal cardiac events

    mhra · safety · mhra · via carfilzomib

  7. Accelerated approval granted2015-11-19

    Accelerated approval: Kyprolis (EMA)

    ema · regulatory · ema · via carfilzomib

  8. Regulatory approval2015-07-20

    Approval: Bortezomib Accord (EMA)

    ema · regulatory · ema · via bortezomib

  9. New publication2011-08-01
    Proteasome inhibition in myelodysplastic syndromes and acute myelogenous leukemia cell lines.

    Cancer investigation · 2011 · 12 citations · Europe PMC · via bortezomib

  10. New publication2011-02-21
    Weekly bortezomib in combination with temsirolimus in relapsed or relapsed and refractory multiple myeloma: a multicentre, phase 1/2, open-label, dose-escalation study.

    The Lancet. Oncology · 2011 · 66 citations · Europe PMC · via bortezomib

  11. New publication2010-12-14
    Phase 2 trial of rituximab and bortezomib in patients with relapsed or refractory mantle cell and follicular lymphoma.

    Cancer · 2011 · 31 citations · Europe PMC · via bortezomib

  12. New publication2010-02-08
    Phase II trial of weekly bortezomib in combination with rituximab in relapsed or relapsed and refractory Waldenstrom macroglobulinemia.

    Journal of clinical oncology : official journal of the American Society of Clinical Oncology · 2010 · 112 citations · Europe PMC · via bortezomib

Objective event titles are shown unmodified; the event kind and significance line are derived from structured fields. Forefront AttentionEvent stream aggregating Europe PMC Regulatory filings ClinicalTrials.gov.