Back to discover
Disease

Li-Fraumeni Syndrome

Active therapeutic pipelineEmerging research
1
Publications
2
Clinical trials
2020
Latest publication
Latest activity
beta

Recent clinical, regulatory, research and industry developments relating to this disease.

Guidelines for the Li-Fraumeni and heritable TP53-related cancer syndromes.

Research2020-05-26European journal of human genetics : EJHG

What's happening now

An analyst briefing on current research, clinical, regulatory and industry activity surrounding this disease.

No activity recorded in this window. Try a wider timeframe.

Clinical trials

2 sponsors · 0 new · 0 completed in the last 12 months (net +0)

The current development programme across all trial phases.

Clinical programme
2
All trials
1
Active
0
Late-stage
1
Completed
Recently completed

A Pilot Study of Metformin in Patients With a Diagnosis of Li-Fraumeni Syndrome

Phase 1 · Completed · National Cancer Institute (NCI)

Research activity

1 papers

Key research shaping understanding of this disease, combining the latest publications with the most influential evidence.

Most influential

Guidelines for the Li-Fraumeni and heritable TP53-related cancer syndromes.

European journal of human genetics : EJHG · 2020 · 232 cites
Recent publications

Guidelines for the Li-Fraumeni and heritable TP53-related cancer syndromes.

European journal of human genetics : EJHG · 2020 · 232 cites
Leading journals1
  • European journal of human genetics : EJHG1
Leading researchers5
  • Bajalica Lagercrantz S1
  • Evans DG1
  • Frebourg T1
  • Magenheim R1
  • Oliveira C1
Affiliations (unnormalised)4
  • Department of Clinical Genetics1
  • i3S-Instituto de Investigação e Inovação em Saúde & Institute of Molecular Pathology and Immunology of the University of Porto1
  • Manchester Centre for Genomic Medicine1
  • Rouen University Hospital and Inserm U12451

Reference

Authoritative identity, definition & identifiers.

Defined in MeSH

Rare autosomal dominant syndrome characterized by mesenchymal and epithelial neoplasms at multiple sites. MUTATION of the p53 tumor suppressor gene, a component of the DNA DAMAGE response pathway, apparently predisposes family members who inherit it to develop certain cancers. The spectrum of cancers in the syndrome was shown to include, in addition to BREAST CANCER and soft tissue sarcomas (SARCOMA); BRAIN TUMORS; OSTEOSARCOMA; LEUKEMIA; and ADRENOCORTICAL CARCINOMA.

References & data sources
  • Disease identity & definition — NLM Medical Subject Headings (MeSH), public domain
  • Clinical trials — ClinicalTrials.gov (U.S. National Library of Medicine)
  • Research activity — Europe PMC (EMBL-EBI) + OpenAlex-derived paper links
  • Related entities are derived from literature co-mention (studied together) — associative, not causal.